Gene Replacement for Rett Syndrome 101
Gene therapy is one of six strategies we’re pursuing at RSRT that attacks the underlying genetic error in Rett syndrome. Gene replacement is the closest to clinical trials and, if those trials are successful, the clinic. Learn more from one of our recent webinars about what gene replacement entails, its challenges, and how we hope to bring gene therapy to Rett families. If you have questions about gene replacement for Rett, this webinar is where you’ll get the answers. Watch now.