Novartis and gene therapy to treat Rett Syndrome.

Novartis, a multinational biotechnology company, issued a statement in August 2020 to confirm full commitment to their gene therapy program for Rett Syndrome. This was followed by a press release from the company in March 2021 which reported recent results of gene therapy to treat patients with spinal muscular atrophy…

New hope for girls with Rett Syndrome

ANAVEX®2-73 - A drug used to help adult Alzheimer’s patients may offer hope to young girls with Rett syndrome. In a new clinical trial being led by The Children’s Hospital at Westmead, doctors are testing whether ANAVEX®2-73 can help improve some of the devastating features of Rett syndrome including their…
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